Stem cell transplantation for congenital immunodeficiencies using reduced-intensity conditioning

Bone Marrow Transplant. 2005 Mar:35 Suppl 1:S45-7. doi: 10.1038/sj.bmt.1704846.

Abstract

The optimal preparation for stem cell transplantation (SCT) in children with congenital immunodeficiencies is currently unknown. In all, 81 children with immunodeficiency underwent 82 SCTs using reduced-intensity conditioning (RIC). The incidence of significant GVHD was low; viral reactivation was prominent with an unexpected increase in EBV reactivation; immune reconstitution was similar between different donor groups and comparable to conventional SCT. Overall, 68/81 (84%) survive with no significant difference between donor types or between severe combined immunodeficiency (SCID) and non-SCID diseases. Findings suggest a significant survival advantage in the unrelated donor setting for RIC compared to conventional SCT.

MeSH terms

  • Adolescent
  • Child
  • Child, Preschool
  • Female
  • Graft vs Host Disease / mortality
  • Graft vs Host Disease / prevention & control
  • Humans
  • Infant
  • Infant, Newborn
  • Male
  • Severe Combined Immunodeficiency / congenital
  • Severe Combined Immunodeficiency / mortality
  • Severe Combined Immunodeficiency / therapy*
  • Stem Cell Transplantation* / mortality
  • Transplantation Conditioning / methods*
  • Transplantation Conditioning / mortality
  • Transplantation, Homologous