Characteristics of children with SMA
| n (%) | |
| Sex | |
| Female | 5 (33) |
| Male | 10 (67) |
| Age at interview (years) | |
| 0–1 | 2 (13) |
| 2–3 | 4 (27) |
| 4–6 | 1 (7) |
| 7–10 | 5 (33) |
| 11+ | 3 (20) |
| SMA type | |
| 1 | 5 (33) |
| 2 | 5 (33) |
| 3 | 5 (33) |
| Nusinersen | |
| Yes | 14 (93) |
| No | 1 (7) |
| Onasemnogene abeparvovec | |
| Yes | 4 (27) |
| No | 11 (73) |
| Risdiplam | |
| Yes | 2 (13) |
| No | 13 (87) |
| Distance from hospital (km) | |
| 0–25 | 5 (33) |
| 26–50 | 8 (53) |
| 51+ | 2 (13) |
| Ambulatory | |
| Yes | 5 (33) |
| No | 10 (67) |
| Ventilation | |
| Noninvasive ventilation | 3 (20) |
| Invasive ventilation via tracheostomy | 2 (13) |
| None | 10 (67) |
| Mechanical insufflation-exsufflation | |
| Yes | 6 (40) |
| No | 9 (60) |
| Enteral feed | |
| Gastrostomy tube | 4 (27) |
| Gastrojejunostomy tube | 2 (13) |
| None | 9 (60) |
SMA, spinal muscular atrophy.;