Baseline descriptive data
Patient | Gender | Diagnosis | Age | Age at initiation of NPPV (y) | Duration of follow up (y) |
---|---|---|---|---|---|
1 | F | Spinal muscular atrophy type II | 3.83 | 2.6 | 1 |
2 | F | Congenital muscular dystrophy | 11.25 | 7 | 4.2 |
3 | F | Congenital fibre disproportionate type myopathy | 6.21 | 1.1 | 4.9 |
4 | F | Myotonic dystrophy | 15.21 | 13.5 | 1.5 |
5 | F | Fascio-scapular humeral myopathy | 13.4 | 7.9 | 5 |
6 | M | Congenital muscular dystrophy | 13.2 | 10.9 | 1.2 |
7 | F | Myotonic dystrophy | 17.78 | 13.2 | 3 |
8 | M | Spinal muscular atrophy type II | 16.46 | 7 | 8.6 |
9 | M | Duchenne muscular dystrophy | 16.79 | 14.3 | 2.4 |
10 | M | Spinal muscular atrophy type II | 10.22 | 8 | 2 |
11 | M | Nemaline rod myopathy | 14.23 | 5 | 8.5 |
12 | F | Muscular dystrophy | 9.55 | 6.5 | 3 |
13 | F | Nemaline rod myopathy | 3.4 | 2 | 1.3 |
14 | F | Spinal muscular atrophy type II | 6.09 | 0.5 | 4.4 |
15 | M | Charcot Marie tooth myopathy | 17.21 | 10 | 7 |