Table 2

Patient treatment and response

Patient	Sex and current age	Weight at presentation	Current weight and height	Treatment	Current symptoms
1		Female 11 years		6.56 kg Below 10th centile		Weight 3rd centile	Prednisolone continued for 6 months		Exercise limitation
						Height 25th centile

2		Male 10 years		5.58 kg Below 50th centile		Weight 50th centile	Prednisolone continued for 1 year and 3 months		Exercise limitation
						Height 50th centile

3		Male 10 years		3.57 kg Below 3rd centile		Weight 3rd centile	Prednisolone continued for 2 years and 9 months		Exercise limitation
						Height 3rd centile

4		Male 9 years		4.2 kg 50th centile		Weight 50th centile	Prednisolone trial for 3 months only		Well
						Height 50th centile

5		Male 8 years		5.8 kg 3rd centile		Weight 90th centile	Prednisolone continued for 6 years and 3 months, home oxygen		Exercise limitation, nocturnal oxygen
						Height 90th centile

6		Male 6 years		6.5 kg Below 3rd centile		Weight 50th centile	Prednisolone continued for 3 years and 3 months		Well
						Height 50th centile

7		Male 5 years		1.24 kg 50th centile		Weight 50th centile	Prednisolone trial for 3 months only, home oxygen		Exercise limitation
						Height 50th centile

8		Male 5 years		10.18 kg Below 50th centile		Weight 50th centile	Prednisolone trial for 3 months only		Exercise limitation
						Height 50th centile

9		Male 3 years		4.25 kg Below 3rd centile		Weight 3rd centile	Prednisolone trial for 3 months only, home oxygen		Exercise limitation
						Height 10th centile

10		Female 3 years		5.7 kg Below 3rd centile		Weight 3rd centile	Prednisolone continued for 4 months, home oxygen		Oxygen dependent
						Height 10th centile

11		Female 18 months		5.56 kg Below 3rd centile		Weight 3rd centile	Prednisolone for 3 months only, home oxygen, chloroquine		Oxygen dependent
						Head circumference 10th centile