orphan regulation

Comparative analysis of the scope of European Union paediatric investigation plans with corresponding orphan designations
Andrea Ecker, Segundo Mariz, Frauke Naumann-Winter, Koenraad Norga, Ingeborg Barisic, Thomas Girard, Paolo Tomasi, Dirk Mentzer, Bruno Sepodes

Archives of Disease in Childhood May 2018, 103 (5) 427-430; DOI: 10.1136/archdischild-2017-313352

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orphan regulation