Bone marrow transplantation
| Patient | Type of BMT (nucleated cells/kg) | Age at BMT | Conditioning | Engraftment | Complications |
| 1 | Parental (1) | 2.3 years | Bu 16 Cy 200 | No | Graft rejection |
| CyA AZX | |||||
| MUD (2) | Yes | Alive and well at 5 years | |||
| (5.0 × 108/kg) | |||||
| 4 | HLA identical MSD | 15.6 years | Bu 16 Cy 200 | Yes | CMV/adenovirus pneumonitis |
| (3.9 × 108/kg) | CyA AZX | Cryptosporidium | |||
| (died D +93) | |||||
| 7 | HLA identical paternal uncle | 7 months | Campath 1G (D −10 to −6) | No | Acute renal failure (Foscarnet) |
| (4.0 × 108/kg) | Bu 20 Cy 200 | Toxic epidermal necrolysis | |||
| CyA | Disseminated CMV | ||||
| (died D +17) | |||||
| 8 | HLA identical great uncle (1) | 1 month | Bu 16 Cy 200 | Yes transient (D +21) | Transplant associated pneumonitis |
| (11.5 × 108/kg) | ATG (D −4 to −1) | Transplant rejection | |||
| DQ mismatched paternal uncle (2) | CyA, MTX×3 | ||||
| (T cell depleted) | 5 months | Bu 20 Cy 200 | Yes (D +14) | Transplant associated pneumonitis | |
| (5.5 × 108/kg) | anti-LFA-1/CD2 | Rotavirus enteritis | |||
| (D −3 to +10) | (died D +87) | ||||
| 9 | HLA identical sister | 6 months | Bu 20 Cy 200 | No | Parainfluenza III pneumonitis |
| (7.8 × 108/kg) | CyA MTX×2 | (died D +19) | |||
| 10 | HLA identical father | 6 years | Flu, Mel | Yes | Severe gastroenteritis |
| (whole marrow) | Cryptosporidium, adeno CMV viraemia | ||||
| (8.4 × 108/kg) | (asymptomatic) | ||||
| (alive 5 months post-BMT) | |||||
Bu 20, busulphan total dose 20 mg/kg given as 4 divided doses (5 mg/kg) over 4 days; Cy 200, cyclophosphamide total dose 200 mg/kg given as 4 divided doses (50 mg/kg) over 4 days; AZX, azathioprine; MTX, methotrexate; Flu, fludarabine 30 mg/m2; Mel, melphalan 140 mg/m2.